rare disease international
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...make Alnylam's therapies available in additional international ... offering newfound hope for patients suffering from rare diseases." ...RNA (mRNA) - the genetic precursors - that encode for disease - ...
Adnkronos
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30-4-2024
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... RARE - rare and ultra - rare diseases, and CARE - specialty care,... Europe at 7% and China and International at 22%). The focus on ...treatment of asthma and COPD (Chronic Obstructive Pulmonary Disease)...
Adnkronos
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22-4-2024
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